Table 1 Infusion therapy in patients with MPS II
From: Home treatment in paediatric patients with Hunter syndrome: the first Italian experience
Patient 1 | Patient 2 | Patient 3 | |
|---|---|---|---|
Age at diagnosis | 4 y 9 mo | 1 y 8 mo | 7 y 8 mo |
Phenotype | severe | severe | mild |
Age at start of ERT | 4 y 11 mo | 2 y 5 mo | 11 y 3 mo |
ERT at hospital (number of infusions) | 69 | 157 | 128 |
ADRs at hospital | 0 | 2 | 1 |
Age at start of ERT at home | 6 y 4 mo | 6 y 2 mo | 16 y 2 mo |
ERT at home (number of infusions) | 87 | 73 | 74 |
ADRs at home | 0 | 0 | 0 |