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Table 1 Infusion therapy in patients with MPS II

From: Home treatment in paediatric patients with Hunter syndrome: the first Italian experience

  Patient 1 Patient 2 Patient 3
Age at diagnosis 4 y 9 mo 1 y 8 mo 7 y 8 mo
Phenotype severe severe mild
Age at start of ERT 4 y 11 mo 2 y 5 mo 11 y 3 mo
ERT at hospital (number of infusions) 69 157 128
ADRs at hospital 0 2 1
Age at start of ERT at home 6 y 4 mo 6 y 2 mo 16 y 2 mo
ERT at home (number of infusions) 87 73 74
ADRs at home 0 0 0
  1. ADR adverse drug reaction, ERT enzyme replacement therapy.